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INS1203: RNA-End Joining Technology Enables A Dual AAV Approach for ABCA4 Gene Replacement in Stargardt Disease

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Speaker Presentation: CGTP 2025
Hilde Kathryn, Insmed Incorporated, 2025
INS1203: RNA-End Joining Technology Enables A Dual AAV Approach for ABCA4 Gene Replacement in Stargardt Disease