
INS1203: RNA-End Joining Technology Enables A Dual AAV Approach for ABCA4 Gene Replacement in Stargardt Disease

Speaker Presentation: CGTP 2025
Hilde Kathryn, Insmed Incorporated, 2025
INS1203: RNA-End Joining Technology Enables A Dual AAV Approach for ABCA4 Gene Replacement in Stargardt Disease